Hot Topic Symposia

The Adrian Spitzer Lectureship: Novel Mechanistic and Therapeutic Discoveries in Rare Diseases

Autologous Transplantation of Gene-modified Hematopoietic Stem Cells for cystinosis: updates from a phase I/II clinical trial

Sunday, April 24, 2022

9:00 AM – 9:20 AM US MT

Location: Convention Center: 708/710/712

CE: Enduring CME: 0.25

Speaker(s)

Stephanie N. Cherqui, PhD
Associate Professor
University of California, San Diego
La Jolla, California, United States

Full Presentation

Participants should be aware of the following financial/non-financial relationships:

Stephanie N. Cherqui, PhD: ● AVROBIO, Inc (Currently Ongoing) (Products/Services: Consultant, Advisory Committee).
● Papillon Therapeutics (Currently Ongoing) (Products/Services: Intellectual Property including patent beneficiary and royalties, Board Member or Executive Role, Ownership Interest including individual stocks, stock options, excluding diversified mutual funds).